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Gene Therapy Trials
Gene Therapy Trials
The research and development for Gene Therapy Trials in France, U.K. and U.S.A. is sponsored by the French Muscular Dystrophy Association (AFM), raising funds for rare diseases through the annual telethon in France. AFM funds the Genethon laboratory which has conducted the pharmaceutical development and sponsors the U.K. and French trials.
Contact Information:
France
- Alain Fischer, M.D. PhD E Mail: Fischer@necker.fr, alain.fischer@nck.ap-hop-paris.fr
- Marina Cavazzana-Calvo PhD E Mail: m.cavazzana@nck.ap-hop-paris.fr
- Anne Galy, Pharm D, PhD E Mail: galy@genethon.fr
Germany
Italy
- Maria Grazia Roncarolo, M.D., PhD. E Mail: roncarolo.mariagrazia@hsr.it
- Alessandro Aiuti M.D. PhD E Mail: aiuti.alessandro@hsr.it
U.K.
- Adrian Thrasher, M.D., PhD E Mail: A.Thrasher@ich.ucl.ac.uk
U.S.A.
- David A. Williams, M.D. E Mail: DAWilliams@childrens.harvard.edu
- Sung-Yun Pai, M.D. E Mail: sung-yun.pai@childrens.harvard.edu
- Luigi Notarangelo, M.D E Mail: luigi.notarangelo@childrens.harvard.edu
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